Research Article| Volume 30, P105-107, January 2021

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A Decision for Life – Treatment decisions in newly diagnosed families with spinal muscular atrophy (SMA)

Published:December 14, 2020DOI:


      • With several treatments available, families with a child with SMA are faced with challenging decisions.
      • In order to make informed decisions, families need to understand the full picture of the disease, including the patient perspective on quality of life.
      • A transparent discussion about the range of potential outcomes of different treatments, followed by shared decision-making is essential.
      • Predictive factors for treatment outcomes remain unclear, therefore potential treatment benefit must be assessed on an individual level.
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